| Lvl | Code | Display | Definition |
| 1 |
summaries |
CTD Summaries |
Module 2 – CTD Summaries |
| 2 |
summaries.quality |
Quality Overall Summary |
2.3 Quality Overall Summary |
| 3 |
summaries.quality.intro |
Introduction |
2.3.S/P Introduction |
| 3 |
summaries.quality.body |
Body of Data |
2.3.S/P Body of Data |
| 3 |
summaries.quality.literature |
Literature References |
2.3.S/P Literature References |
| 2 |
summaries.nonclinical |
Nonclinical Overview |
2.4 Nonclinical Overview |
| 3 |
summaries.nonclinical.pharmacology |
Pharmacology |
2.4.1-2 Pharmacology |
| 3 |
summaries.nonclinical.pk |
Pharmacokinetics |
2.4.3 Pharmacokinetics |
| 3 |
summaries.nonclinical.tox |
Toxicology |
2.4.4-6 Toxicology |
| 2 |
summaries.clinical |
Clinical Overview |
2.5 Clinical Overview |
| 3 |
summaries.clinical.efficacy |
Efficacy |
2.5.2 Efficacy |
| 3 |
summaries.clinical.safety |
Safety |
2.5.3 Safety |
| 3 |
summaries.clinical.brm |
Benefit-Risk Assessment |
2.5.4 Benefit-Risk |
| 2 |
summaries.synopses |
Synopses of Individual Studies |
2.7 Synopses of Individual Studies |
| 1 |
quality |
Quality (CMC) |
Module 3 – Quality |
| 2 |
quality.drug-substance |
Drug Substance |
3.2.S Drug Substance |
| 3 |
quality.drug-substance.general |
General Information |
3.2.S.1 General Information |
| 4 |
quality.drug-substance.general.nomenclature |
Nomenclature |
3.2.S.1.1 Nomenclature |
| 4 |
quality.drug-substance.general.structure |
Structure |
3.2.S.1.2 Structure |
| 4 |
quality.drug-substance.general.properties |
General Properties |
3.2.S.1.3 General Properties |
| 3 |
quality.drug-substance.manufacture |
Manufacture |
3.2.S.2 Manufacture |
| 4 |
quality.drug-substance.manufacture.manufacturer |
Manufacturer |
3.2.S.2.1 Manufacturer |
| 4 |
quality.drug-substance.manufacture.description |
Description of Manufacturing Process and Process Controls |
3.2.S.2.2 Description of Manufacturing Process |
| 4 |
quality.drug-substance.manufacture.controls |
Control of Materials |
3.2.S.2.3 Control of Materials |
| 4 |
quality.drug-substance.manufacture.critical-steps |
Controls of Critical Steps and Intermediates |
3.2.S.2.4 Controls of Critical Steps and Intermediates |
| 4 |
quality.drug-substance.manufacture.validation |
Process Validation and/or Evaluation |
3.2.S.2.5 Process Validation |
| 4 |
quality.drug-substance.manufacture.development |
Manufacturing Process Development |
3.2.S.2.6 Manufacturing Process Development |
| 3 |
quality.drug-substance.characterisation |
Characterisation |
3.2.S.3 Characterisation |
| 4 |
quality.drug-substance.characterisation.elucidation |
Elucidation of Structure and Other Characteristics |
3.2.S.3.1 Elucidation of Structure |
| 4 |
quality.drug-substance.characterisation.impurities |
Impurities |
3.2.S.3.2 Impurities |
| 3 |
quality.drug-substance.control |
Control of Drug Substance |
3.2.S.4 Control of Drug Substance |
| 4 |
quality.drug-substance.control.specification |
Specification |
3.2.S.4.1 Specification |
| 4 |
quality.drug-substance.control.analytical |
Analytical Procedures |
3.2.S.4.2 Analytical Procedures |
| 4 |
quality.drug-substance.control.validation |
Validation of Analytical Procedures |
3.2.S.4.3 Validation of Analytical Procedures |
| 4 |
quality.drug-substance.control.batch |
Batch Analyses |
3.2.S.4.4 Batch Analyses |
| 4 |
quality.drug-substance.control.justification |
Justification of Specification |
3.2.S.4.5 Justification of Specification |
| 3 |
quality.drug-substance.reference |
Reference Standards or Materials |
3.2.S.5 Reference Standards |
| 3 |
quality.drug-substance.container |
Container Closure System |
3.2.S.6 Container Closure System |
| 3 |
quality.drug-substance.stability |
Stability |
3.2.S.7 Stability |
| 4 |
quality.drug-substance.stability.summary |
Stability Summary and Conclusions |
3.2.S.7.1 Stability Summary |
| 4 |
quality.drug-substance.stability.protocol |
Post-approval Stability Protocol and Commitment |
3.2.S.7.2 Post-approval Protocol |
| 4 |
quality.drug-substance.stability.data |
Stability Data |
3.2.S.7.3 Stability Data |
| 2 |
quality.drug-product |
Drug Product |
3.2.P Drug Product |
| 3 |
quality.drug-product.description |
Description and Composition of the Drug Product |
3.2.P.1 Description and Composition |
| 3 |
quality.drug-product.pharmaceutical-development |
Pharmaceutical Development |
3.2.P.2 Pharmaceutical Development |
| 4 |
quality.drug-product.pharmaceutical-development.components |
Components of the Drug Product |
3.2.P.2.1 Components |
| 4 |
quality.drug-product.pharmaceutical-development.drug-product |
Drug Product |
3.2.P.2.2 Drug Product |
| 4 |
quality.drug-product.pharmaceutical-development.manufacturing |
Manufacturing Process Development |
3.2.P.2.3 Manufacturing Process Development |
| 4 |
quality.drug-product.pharmaceutical-development.container |
Container Closure System |
3.2.P.2.4 Container Closure System |
| 4 |
quality.drug-product.pharmaceutical-development.microbiological |
Microbiological Attributes |
3.2.P.2.5 Microbiological Attributes |
| 4 |
quality.drug-product.pharmaceutical-development.compatibility |
Compatibility |
3.2.P.2.6 Compatibility |
| 3 |
quality.drug-product.manufacture |
Manufacture |
3.2.P.3 Manufacture |
| 4 |
quality.drug-product.manufacture.manufacturer |
Manufacturer(s) |
3.2.P.3.1 Manufacturer(s) |
| 4 |
quality.drug-product.manufacture.batch |
Batch Formula |
3.2.P.3.2 Batch Formula |
| 4 |
quality.drug-product.manufacture.process |
Description of Manufacturing Process and Process Controls |
3.2.P.3.3 Description of Manufacturing Process |
| 4 |
quality.drug-product.manufacture.controls |
Controls of Critical Steps and Intermediates |
3.2.P.3.4 Controls of Critical Steps |
| 4 |
quality.drug-product.manufacture.validation |
Process Validation and/or Evaluation |
3.2.P.3.5 Process Validation |
| 3 |
quality.drug-product.excipients |
Control of Excipients |
3.2.P.4 Control of Excipients |
| 4 |
quality.drug-product.excipients.specifications |
Specifications |
3.2.P.4.1 Specifications |
| 4 |
quality.drug-product.excipients.analytical |
Analytical Procedures |
3.2.P.4.2 Analytical Procedures |
| 4 |
quality.drug-product.excipients.validation |
Validation of Analytical Procedures |
3.2.P.4.3 Validation |
| 4 |
quality.drug-product.excipients.justification |
Justification of Specifications |
3.2.P.4.4 Justification |
| 4 |
quality.drug-product.excipients.novel |
Novel Excipients |
3.2.P.4.5 Novel Excipients |
| 3 |
quality.drug-product.control |
Control of Drug Product |
3.2.P.5 Control of Drug Product |
| 4 |
quality.drug-product.control.specification |
Specification |
3.2.P.5.1 Specification |
| 4 |
quality.drug-product.control.analytical |
Analytical Procedures |
3.2.P.5.2 Analytical Procedures |
| 4 |
quality.drug-product.control.validation |
Validation of Analytical Procedures |
3.2.P.5.3 Validation |
| 4 |
quality.drug-product.control.batch |
Batch Analyses |
3.2.P.5.4 Batch Analyses |
| 4 |
quality.drug-product.control.characterisation |
Characterisation of Impurities |
3.2.P.5.5 Characterisation of Impurities |
| 4 |
quality.drug-product.control.justification |
Justification of Specification |
3.2.P.5.6 Justification |
| 3 |
quality.drug-product.reference |
Reference Standards or Materials |
3.2.P.6 Reference Standards |
| 3 |
quality.drug-product.container |
Container Closure System |
3.2.P.7 Container Closure System |
| 3 |
quality.drug-product.stability |
Stability |
3.2.P.8 Stability |
| 4 |
quality.drug-product.stability.summary |
Stability Summary and Conclusions |
3.2.P.8.1 Stability Summary |
| 4 |
quality.drug-product.stability.protocol |
Post-approval Stability Protocol and Commitment |
3.2.P.8.2 Post-approval Protocol |
| 4 |
quality.drug-product.stability.data |
Stability Data |
3.2.P.8.3 Stability Data |
| 2 |
quality.appendices |
Appendices |
3.2.A Appendices |
| 3 |
quality.appendices.facilities |
Facilities and Equipment |
3.2.A.1 Facilities and Equipment |
| 3 |
quality.appendices.adventitious |
Adventitious Agents Safety Evaluation |
3.2.A.2 Adventitious Agents |
| 3 |
quality.appendices.novel-excipients |
Novel Excipients |
3.2.A.3 Novel Excipients |
| 2 |
quality.regional |
Regional Information |
3.3 Regional Information |
| 1 |
nonclinical |
Nonclinical Study Reports |
Module 4 – Nonclinical Study Reports |
| 2 |
nonclinical.pharmacology |
Pharmacology |
4.2 Pharmacology |
| 3 |
nonclinical.pharmacology.primary |
Primary Pharmacodynamics |
4.2.1.1 Primary Pharmacodynamics |
| 3 |
nonclinical.pharmacology.secondary |
Secondary Pharmacodynamics |
4.2.1.2 Secondary Pharmacodynamics |
| 3 |
nonclinical.pharmacology.safety |
Safety Pharmacology |
4.2.1.3 Safety Pharmacology |
| 3 |
nonclinical.pharmacology.discussion |
Pharmacodynamic Drug Interactions |
4.2.1.4 Pharmacodynamic Drug Interactions |
| 2 |
nonclinical.pk |
Pharmacokinetics |
4.2.2 Pharmacokinetics |
| 3 |
nonclinical.pk.absorption |
Absorption |
4.2.2.1 Absorption |
| 3 |
nonclinical.pk.distribution |
Distribution |
4.2.2.2 Distribution |
| 3 |
nonclinical.pk.metabolism |
Metabolism |
4.2.2.3 Metabolism |
| 3 |
nonclinical.pk.excretion |
Excretion |
4.2.2.4 Excretion |
| 3 |
nonclinical.pk.interactions |
PK Drug Interactions |
4.2.2.5 PK Drug Interactions |
| 2 |
nonclinical.toxicology |
Toxicology |
4.2.3 Toxicology |
| 3 |
nonclinical.toxicology.single |
Single-Dose Toxicity |
4.2.3.1 Single-Dose Toxicity |
| 3 |
nonclinical.toxicology.repeat |
Repeat-Dose Toxicity |
4.2.3.2 Repeat-Dose Toxicity |
| 3 |
nonclinical.toxicology.geno |
Genotoxicity |
4.2.3.3 Genotoxicity |
| 4 |
nonclinical.toxicology.geno.invitro |
In Vitro |
4.2.3.3.1 In Vitro |
| 4 |
nonclinical.toxicology.geno.invivo |
In Vivo |
4.2.3.3.2 In Vivo |
| 3 |
nonclinical.toxicology.carc |
Carcinogenicity |
4.2.3.4 Carcinogenicity |
| 3 |
nonclinical.toxicology.repro |
Reproductive and Developmental Toxicity |
4.2.3.5 Reproductive Toxicity |
| 4 |
nonclinical.toxicology.repro.fertility |
Fertility and Early Embryonic Development |
4.2.3.5.1 Fertility |
| 4 |
nonclinical.toxicology.repro.embryo |
Embryo-Fetal Development |
4.2.3.5.2 Embryo-Fetal |
| 4 |
nonclinical.toxicology.repro.peri |
Peri- and Post-Natal Development |
4.2.3.5.3 Peri-/Post-Natal |
| 3 |
nonclinical.toxicology.local |
Local Tolerance |
4.2.3.6 Local Tolerance |
| 3 |
nonclinical.toxicology.other |
Other Toxicity Studies |
4.2.3.7 Other Toxicity Studies |
| 4 |
nonclinical.toxicology.other.antigenicity |
Antigenicity |
4.2.3.7.1 Antigenicity |
| 4 |
nonclinical.toxicology.other.immunotox |
Immunotoxicity |
4.2.3.7.2 Immunotoxicity |
| 4 |
nonclinical.toxicology.other.mechanistic |
Mechanistic Studies |
4.2.3.7.3 Mechanistic |
| 4 |
nonclinical.toxicology.other.impurities |
Impurities |
4.2.3.7.4 Impurities |
| 4 |
nonclinical.toxicology.other.metabolites |
Metabolites |
4.2.3.7.5 Metabolites |
| 4 |
nonclinical.toxicology.other.other |
Other |
4.2.3.7.6 Other |
| 1 |
clinical |
Clinical Study Reports |
Module 5 – Clinical Study Reports |
| 2 |
clinical.biopharm |
Biopharmaceutic Studies |
5.2 Biopharmaceutic Studies |
| 3 |
clinical.biopharm.ba-be |
Bioavailability / Bioequivalence |
5.2.1-2 BA/BE Studies |
| 3 |
clinical.biopharm.invitro |
In Vitro–In Vivo Correlation |
5.2.3 IVIVC |
| 2 |
clinical.pk |
Clinical Pharmacology Studies |
5.3 Clinical Pharmacology |
| 3 |
clinical.pk.healthy |
Studies in Healthy Subjects |
5.3.1 Healthy Subjects |
| 3 |
clinical.pk.patient |
Studies in Target Population |
5.3.2 Target Population |
| 3 |
clinical.pk.intrinsic |
Intrinsic Factors |
5.3.3 Intrinsic Factors |
| 4 |
clinical.pk.intrinsic.renal |
Renal Impairment |
5.3.3.1 Renal |
| 4 |
clinical.pk.intrinsic.hepatic |
Hepatic Impairment |
5.3.3.2 Hepatic |
| 4 |
clinical.pk.intrinsic.age |
Age / Pediatric |
5.3.3.3 Age/Pediatric |
| 3 |
clinical.pk.extrinsic |
Extrinsic Factors |
5.3.4 Extrinsic Factors |
| 4 |
clinical.pk.extrinsic.ddi |
Drug-Drug Interactions |
5.3.4.1 DDI |
| 3 |
clinical.pk.pop |
Population PK |
5.3.5 Population PK |
| 2 |
clinical.efficacy |
Clinical Efficacy & Safety Studies |
5.3.5-5.4 Efficacy and Safety |
| 3 |
clinical.efficacy.controlled |
Controlled Clinical Studies |
5.3.5.1 Controlled Studies |
| 3 |
clinical.efficacy.uncontrolled |
Uncontrolled Studies |
5.3.5.2 Uncontrolled |
| 3 |
clinical.efficacy.other |
Other Studies |
5.3.5.3 Other |
| 3 |
clinical.efficacy.analysis |
Analyses of Efficacy |
5.3.5.4 Analyses |
| 2 |
clinical.safety |
Safety Data |
5.3.6 Safety |
| 3 |
clinical.safety.exposure |
Extent of Exposure |
5.3.6.1 Exposure |
| 3 |
clinical.safety.ae |
Adverse Events |
5.3.6.2 AEs |
| 3 |
clinical.safety.lab |
Clinical Laboratory |
5.3.6.3 Lab |
| 3 |
clinical.safety.vital |
Vital Signs / ECG |
5.3.6.4 Vital/ECG |
| 3 |
clinical.safety.immuno |
Immunogenicity |
5.3.6.5 Immunogenicity |
| 2 |
clinical.literature |
Literature References |
5.4 Literature References |
| 2 |
clinical.synopses |
Synopses of Individual Studies |
5.3.7 Synopses |